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International Journal of Molecular Sciences

ISSN 1422-0067

34 papers in the library · 1,124 citations · publishing 2016-2026

Papers

A Single Dose of Psilocybin Increases Synaptic Density and Decreases 5-HT2A Receptor Density in the Pig Brain

International Journal of Molecular Sciences January 15, 2021 Nakul Ravi Raval, Annette Johansen, Lene Lundgaard Donovan et al. 191 citations

A single psychedelic dose of psilocybin increases synaptic density and temporarily reduces serotonin 2A receptor density in the pig brain. One day after injection, hippocampal synaptic vesicle protein 2A (SV2A) density was 4.42% higher, while hippocampal and prefrontal cortex 5-HT2AR density dropped by 15.21% to 50.19%. Seven days later, SV2A density remained significantly higher in the hippocampus (+9.24%) and prefrontal cortex (+6.10%), but 5-HT2AR density had returned to baseline. These persistent synaptic changes and acute receptor down-regulation may underlie psilocybin’s antidepressant effects.

d-Lysergic Acid Diethylamide (LSD) as a Model of Psychosis: Mechanism of Action and Pharmacology

International Journal of Molecular Sciences November 23, 2016 Danilo de Gregorio, Stefano Comai, Luca Posa et al. 125 citations

LSD produces hallucinogenic and psychotic-like effects through a complex mechanism involving multiple neurotransmitter systems. The primary action occurs in the Dorsal Raphe via the serotonergic system, where LSD acts as a partial agonist at 5-HT2A receptors and an agonist at 5-HT1A receptors. At higher doses, it also stimulates dopamine D2 receptors, Trace Amine Associated Receptor 1 (TAAR1), and 5-HT2A in the Ventral Tegmental Area. This pleiotropic mechanism, engaging serotonergic, dopaminergic, and glutamatergic pathways, makes LSD-induced psychosis a useful preclinical model for testing novel antipsychotic drugs, especially those targeting dual serotonergic and dopaminergic systems or TAAR1 receptors. More human studies are needed to clarify these mechanisms.

Effect of Psilocybin and Ketamine on Brain Neurotransmitters, Glutamate Receptors, DNA and Rat Behavior

International Journal of Molecular Sciences June 16, 2022 Adam Wojtas, Agnieszka Bysiek, Agnieszka Wawrzczak‐bargieła et al. 110 citations

Ketamine and psilocybin, both fast-acting antidepressants in clinical studies, increase extracellular levels of dopamine, serotonin, glutamate, and GABA in the rat frontal cortex. Psilocybin also raises GABA in the reticular nucleus of the thalamus. However, both drugs cause oxidative DNA damage—psilocybin in the frontal cortex and both drugs in the hippocampus. Psilocybin at 10 mg/kg increases NR2A glutamate receptor subunit levels. Behavioral tests 24 hours after administration show no antidepressant or anxiolytic effects; only ketamine reduces locomotor activity. The observed neurotransmitter changes may lead to genotoxicity and altered receptor levels without markedly affecting behavior.

Biomolecular Basis of Cellular Consciousness via Subcellular Nanobrains

International Journal of Molecular Sciences March 3, 2021 František Baluška, William B. Miller, Arthur S. Reber 96 citations

Consciousness and sentience are not exclusive to animals with nervous systems but are grounded in the fundamental biology of all cells. The cellular basis of consciousness (CBC) model proposes that the excitable plasma membrane, which defines a cell's internal and external domains, is the foundation for biological awareness. This article examines the biomolecular structures and processes that enable and sustain this cellular consciousness from an evolutionary perspective, arguing that unicellular organisms like protists and algae, as well as the cells of multicellular fungi, plants, and animals, all possess a primitive form of sentience rooted in general cell biology.

Role of 5-HT2A, 5-HT2C, 5-HT1A and TAAR1 Receptors in the Head Twitch Response Induced by 5-Hydroxytryptophan and Psilocybin: Translational Implications

International Journal of Molecular Sciences November 16, 2022 Orr Shahar, Alexander Botvinnik, Noam Esh-Zuntz et al. 60 citations

Psilocybin and the serotonin precursor 5-HTP produce a characteristic head twitch response in mice, which is linked to the human psychedelic experience. This response depends primarily on the 5-HT2A receptor, as blocking it with M100907 reduced twitching. Activating the 5-HT1A receptor with 8-OH-DPAT also suppressed the response, while blocking the 5-HT2C receptor with RS-102221 had a bimodal effect—enhancing twitching at lower doses but reducing it at higher doses. Blocking the trace amine-associated receptor 1 (TAAR1) with EPPTB reduced 5-HTP-induced twitching but not psilocybin-induced twitching. These findings highlight multiple receptor systems that could modulate psychedelic effects and may inform therapeutic applications.

Overcoming Depression with 5-HT2A Receptor Ligands

International Journal of Molecular Sciences December 21, 2021 Agata Zięba, Piotr Stępnicki, Dariusz Matosiuk et al. 55 citations

Depression affects millions globally and current treatments are not fully curative. Recent insights into the structure and function of the serotonin 2A (5-HT2A) receptor have enabled the design of new antidepressant compounds. This review summarizes the role of 5-HT2A receptor signaling modulators in depression treatment, describes the receptor's structural and physiological features, and overviews recent virtual screening campaigns that identified novel 5-HT2A receptor ligands, along with data on newly synthesized ligands acting through this protein.

Extensive Collection of Psychotropic Mushrooms with Determination of Their Tryptamine Alkaloids

International Journal of Molecular Sciences November 15, 2022 Klára Gotvaldová, Jan Borovička, Kateřina Hájková et al. 50 citations

Wild mushrooms that contain psilocybin also carry several other tryptamine alkaloids in highly variable concentrations, making their effects unpredictable compared to pure psilocybin. Using ultra-high performance liquid chromatography with tandem mass spectrometry, researchers measured psilocybin, psilocin, baeocystin, norbaeocystin, and aeruginascin in 226 fruiting bodies from 82 collections across seven genera. Psilocybe species had the highest psilocybin and psilocin levels, but no tryptamines were detected in Psilocybe fuscofulva or Psilocybe fimetaria. For many species, concentrations of baeocystin, norbaeocystin, and aeruginascin were reported for the first time. The extreme variability in tryptamine content poses a risk of overdose for consumers and complicates interpretation of medicinal effects compared to chemically pure psilocybin.

Toxicology and Analysis of Psychoactive Tryptamines

International Journal of Molecular Sciences December 4, 2020 Sara Malaca, Alfredo Fabrizio Lo Faro, Alice Tamborra et al. 48 citations

Tryptamines are 5-HT2A receptor agonists that alter perceptions of reality. Their prevalence in drug overdoses is low but increasing, yet they are not part of typical toxicology testing, so their contribution may be underestimated. From 2015 to 2020, 22 new analytical methods, primarily liquid chromatography tandem mass spectrometry, were developed to identify tryptamines and metabolites in biological samples. The most prevalent tryptamines are 5-MeO-DiPT, 5-MeO-DALT, and DMT. Morbidity from tryptamine intake is considerable, and clinicians and laboratorians need updated data on this public health threat.

The Bright Side of Psychedelics: Latest Advances and Challenges in Neuropharmacology

International Journal of Molecular Sciences January 10, 2023 Andrea Mastinu, Margrate Anyanwu, Marinella Carone et al. 45 citations

Psychedelic compounds such as psilocybin and LSD are being reexamined as potential treatments for psychiatric disorders like depression, obsessive-compulsive disorder, and post-traumatic stress disorder, though clinical results remain unclear and definitive. The mechanisms of action of these molecules are not fully understood. This review summarizes the ethnobotanical uses of well-known psychedelic plants and the pharmacological mechanisms of their active ingredients. It provides an overview of structural and computational studies on the binding of ibogaine, mescaline, DMT, psilocin, and LSD to biological receptors. Recent clinical studies evaluating psychedelics in psychiatric disorders are compared with existing therapies.

Chemistry and Toxicology of Major Bioactive Substances in Inocybe Mushrooms

International Journal of Molecular Sciences February 23, 2021 Jiří Patočka, Ran Wu, Eugenie Nepovimová et al. 45 citations

Mushroom poisoning remains a global health concern, with numerous annual reports of poisonous mushroom ingestion. This review focuses on the genus Inocybe, which contains toxic substances such as muscarine, psilocybin, psilocin, aeruginascin, lectins, and baeocystin. The article summarizes the chemistry, toxic effects, and mechanisms of these major toxins, particularly muscarine, psilocybin, and psilocin, drawing on previously published toxicity data from different species and administration routes. It also discusses treatment options and potential medical applications of these bioactive compounds, aiming to improve understanding of Inocybe toxicology and support future clinical benefits.

Esketamine and Psilocybin—The Comparison of Two Mind-Altering Agents in Depression Treatment: Systematic Review

International Journal of Molecular Sciences September 28, 2022 Dominika Psiuk, Emilia Magdalena Nowak, Natalia Dycha et al. 36 citations

A systematic review of 12 studies examined two psychoactive compounds, psilocybin and esketamine, for treating depression. Esketamine, a laboratory-made substance, showed significant reduction in depressive symptoms and suicidal ideation shortly after intake and after one month, compared to baseline and standard antidepressants. Psilocybin, a naturally occurring psychedelic, produced antidepressant effects one day after intake and after 6–7 weeks, with benefits lasting up to 6 or 8 months. One study suggested psilocybin's effects are comparable to and may be superior to escitalopram. Both compounds demonstrated rapid and sustained effects, indicating potential as novel antidepressant agents after addressing limitations.

The Pharmacological Profile of Second Generation Pyrovalerone Cathinones and Related Cathinone Derivative

International Journal of Molecular Sciences July 31, 2021 Karolina E. Kolaczynska, Jan Thomann, Marius C. Hoener et al. 35 citations

Pyrovalerone cathinones, a class of potent psychoactive substances, were tested for their effects on monoamine transporters and receptors. All tested compounds strongly inhibited the dopamine and norepinephrine transporters, with IC50 values in the low micromolar range, but showed no activity at the serotonin transporter at concentrations below 10 µM. None of the substances triggered monoamine efflux. Two compounds, 4F-PBP and NEH, were particularly selective for the dopamine transporter, suggesting they likely produce strong psychostimulant effects and have high abuse potential. Extending the alkyl chain increased inhibition potency at dopamine and norepinephrine transporters, while a 3,4-methylenedioxy group enhanced serotonin transporter inhibition.

Impact of Two Neuronal Sigma-1 Receptor Modulators, PRE084 and DMT, on Neurogenesis and Neuroinflammation in an Aβ1–42-Injected, Wild-Type Mouse Model of AD

International Journal of Molecular Sciences February 24, 2022 Emőke Borbély, Viktória Varga, Titanilla Szögi et al. 31 citations

Alzheimer's disease (AD), the most common form of dementia, involves cognitive decline. Two sigma-1 receptor (S1R) agonists, dimethyltryptamine (DMT) and PRE084, were tested in a mouse model of AD induced by amyloid-beta (Aβ). DMT, which also binds strongly to serotonin receptors, reduced neurogenesis, likely due to its mixed receptor activity. In contrast, the highly selective S1R agonist PRE084 increased hippocampal cell proliferation and differentiation. Both DMT and PRE084 significantly reduced astrogliosis (a marker of neuroinflammation) caused by Aβ, but neither affected microglial activation. The findings suggest that selective S1R agonists like PRE084 may be promising therapeutic agents for AD, though further research is needed.

Candidate Strategies for Development of a Rapid-Acting Antidepressant Class That Does Not Result in Neuropsychiatric Adverse Effects: Prevention of Ketamine-Induced Neuropsychiatric Adverse Reactions

International Journal of Molecular Sciences October 26, 2020 Motohiro Okada, Yasuhiro Kawano, Kouji Fukuyama et al. 31 citations

Ketamine, an NMDAR antagonist, has been approved for treatment-resistant depression despite its schizophrenia-like side effects. It improves anhedonia, suicidal ideation, and bipolar depression where conventional antidepressants fail. The antidepressant dose is comparable to that producing psychotic symptoms, and psychotropic effects precede antidepressant effects. Repeated administration is often needed but carries risks of abuse and memory deficits. The article reviews clinical evidence for NMDAR antagonists and the temporal mechanisms underlying ketamine's schizophrenia-like and antidepressant-like effects, also discussing rodent pharmacological studies.

Many Drugs of Abuse May Be Acutely Transformed to Dopamine, Norepinephrine and Epinephrine In Vivo

International Journal of Molecular Sciences October 2, 2021 Paul J. Fitzgerald 30 citations

Many drugs of abuse, including stimulants, opioids, psychedelics, and alcohol, may be directly converted in the body into catecholamines—dopamine, norepinephrine, and epinephrine—rather than merely modulating these neurotransmitter systems through receptor binding. This hypothesized transformation could explain both the intoxicating effects and the physiological side effects (elevated heart rate, blood pressure, rapid breathing, increased temperature, sweating, and dilated pupils) typically associated with these substances. If correct, this would revise understanding of catecholamine biosynthesis and the neural basis of substance abuse, dependence, and stress-induced relapse. The hypothesis can be tested by administering stable isotope-labeled drugs to rodents or humans and detecting labeled catecholamines in brain, blood, or urine using liquid chromatography-mass spectrometry.

Methylone and MDMA Pharmacokinetics Following Controlled Administration in Humans

International Journal of Molecular Sciences November 23, 2022 Lourdes Poyatos, Alfredo Fabrizio Lo Faro, Diletta Berardinelli et al. 22 citations

After controlled oral doses of 50–200 mg methylone given to 12 male volunteers, plasma concentrations increased in proportion to dose. Maximum concentrations ranged from 153 ng/mL at the lowest dose to 604 ng/mL at the highest dose. The drug was absorbed rapidly, reaching peak levels in 1.5–2 hours, and had a half-life of about 6 hours. Its metabolite HMMC reached peak concentrations 10–14 times lower than methylone. Unlike MDMA, methylone showed linear pharmacokinetics across the dose range. A validated LC-MS/MS method was used to measure methylone, MDMA, and their metabolites in plasma.

Increased iNOS and Nitrosative Stress in Dopaminergic Neurons of MDMA-Exposed Rats

International Journal of Molecular Sciences March 12, 2019 Stefania Schiavone, Margherita Neri, Angela Bruna Maffione et al. 22 citations

MDMA (ecstasy) neurotoxicity may involve nitrosative stress driven by the enzyme iNOS rather than by NOX enzymes that produce reactive oxygen species. In rats given MDMA, iNOS expression increased, and cells positive for 3-nitrotyrosine (a marker of nitrosative damage) rose in the frontal cortex. No changes occurred in NOX2, NOX1, or NOX4 immunoreactivity or in the oxidative stress marker 8OHdG. MDMA and nitrosative markers colocalized with dopamine-transporter-positive cells, which were neurons, not microglia or astrocytes. The findings indicate that iNOS-derived nitrosative stress, not NOX enzymes, likely contributes to MDMA-induced neurotoxicity.

Molecular and Medical Aspects of Psychedelics

International Journal of Molecular Sciences December 23, 2023 Adam Wojtas, Krystyna Gołembiowska 16 citations

Psychedelics, among the oldest psychoactive drugs, are gaining renewed interest for treating depression, substance use disorders, anxiety, and obsessive-compulsive disorder. This review summarizes preclinical research on the mechanisms, neurotoxicity, and behavioral effects of psychedelics, focusing on the selective 5-HT2A receptor agonists 25I- and 25B-NBOMe compared to the less selective drug psilocybin. NBOMes significantly increased glutamatergic, dopaminergic, serotonergic, and cholinergic neurotransmission in the frontal cortex, striatum, and nucleus accumbens, though not dose-dependently, likely due to 5-HT2A and subsequent 5-HT2C receptor activation.

Limbic System Response to Psilocybin and Ketamine Administration in Rats: A Neurochemical and Behavioral Study

International Journal of Molecular Sciences December 20, 2023 Adam Wojtas, Agnieszka Bysiek, Marzena Maćkowiak et al. 16 citations

Depression involves reduced volume of the hippocampus and amygdala and enlargement of the nucleus accumbens. Ketamine, a fast-acting antidepressant, reverses these volume reductions. This study tested whether the psychedelic psilocybin similarly affects limbic system neurotransmission in rats. Using microdialysis, both psilocybin and ketamine increased dopamine and serotonin release in the nucleus accumbens, influenced glutamate and GABA release in the nucleus accumbens, hippocampus, and amygdala, and raised acetylcholine levels in the hippocampus. Long-lasting changes in D2, 5-HT1A, and 5-HT2A receptor density occurred in the nucleus accumbens and hippocampus. Psilocybin showed a marked anxiolytic effect acutely and 24 hours later in the open field test, providing a neurobiological basis for its antidepressant and anti-stress effects.

A Brief Review on the Potential of Psychedelics for Treating Alzheimer’s Disease and Related Depression

International Journal of Molecular Sciences August 7, 2023 Alexander Pilozzi, Simmie Foster, David Mischoulon et al. 16 citations

Alzheimer's disease, the most common form of senile dementia, will impose a growing societal and healthcare burden as the population ages. With few treatments for symptomatic relief and unknown causes, more research is urgently needed. Psychedelic drugs target AD-related psychological pathology and symptoms such as depression. Through microdosing, they may help combat the disease by eliciting psychiatric benefits via serotonin and dopamine pathways. This review examines studied benefits of a few psychedelic compounds that may show promise in treating AD and attenuating its depressive symptoms. The putative mechanism of action is that psychedelics act mainly as serotonin receptor agonists and induce potential beneficial effects for treating AD and related depression.

Psychedelic-Induced Serotonin 2A Receptor Downregulation Does Not Predict Swim Stress Coping in Mice

International Journal of Molecular Sciences December 4, 2022 Mireia Medrano, An Buckinx, Ilse Smolders et al. 11 citations

Serotoninergic psychedelics like psilocybin can produce lasting reductions in depressive symptoms, but their mechanism is unclear. In a mouse forced swim test model, the psychedelic DOI was tested for effects on behavior and 5-HT2A receptor levels in the medial prefrontal cortex. Mice exposed to swim stress developed passive coping behavior six days later, but this was not linked to increased head twitch responses or consistent changes in 5-HT2A receptor levels. A low dose of DOI (0.2 mg/kg) unexpectedly increased immobility, while a high dose (2 mg/kg) had no significant effect. DOI did cause a dose-dependent decrease in 5-HT2A levels in stressed mice. These results do not support the idea that downregulating 5-HT2A receptors in the medial prefrontal cortex underlies antidepressant-like effects of serotoninergic psychedelics.

Sexually Dimorphic Behavioral Profile in a Transgenic Model Enabling Targeted Recombination in Active Neurons in Response to Ketamine and (2R,6R)-Hydroxynorketamine Administration

International Journal of Molecular Sciences March 20, 2020 David P. Herzog, Ratnadevi M. Mellema, Floortje Remmers et al. 9 citations

In a genetically modified mouse line (Arc-CreERT2 × CAG-Sun1/sfGFP), males and females differed in sociability and anxiety tests. The rapid-acting antidepressants ketamine and (2R,6R)-hydroxynorketamine (HNK) produced opposite effects in the forced swim test depending on sex: in males, ketamine reduced immobility compared to (2R,6R)-HNK, indicating a different behavioral profile between the two drugs. At the molecular level, female mice treated with ketamine showed increased Bdnf mRNA levels, a change previously observed in males.

The Effect of Ketamine on the Immune System in Patients with Treatment-Resistant Depression

International Journal of Molecular Sciences August 1, 2025 Ł. Szałach, Klaudia Ciesielska-Figlon, A. Daca et al. 7 citations

In people with treatment-resistant depression, a single intravenous dose of ketamine (0.5 mg/kg) produces rapid, temporary shifts in immune markers. Within 4 hours, total T cells and certain helper T-cell subsets increased, while by 24 hours, activated T cells declined and the ratio of helper to cytotoxic T cells decreased. Blood levels of the anti-inflammatory cytokine IL-10 rose, while the pro-inflammatory cytokines IL-6 and IL-8 fell—IL-8 remained lower for at least 24 hours. In laboratory experiments, high-dose ketamine boosted the growth of helper T cells from depressed patients and increased secretion of IL-8 and IL-6 from activated immune cells. The sustained drop in IL-8 points to an anti-inflammatory effect and may serve as a biomarker for treatment response.

Substance Abuse and Cognitive Decline: The Critical Role of Tau Protein as a Potential Biomarker

International Journal of Molecular Sciences August 7, 2025 Liliana Rebolledo-Pérez, Jorge Hernández‐bello, Alicia Martínez-ramos et al. 5 citations

Tau protein, essential for neuron stability, becomes toxic when hyperphosphorylated or cleaved, contributing to Alzheimer's disease. Evidence from experimental, clinical, and postmortem studies indicates that chronic substance use alters Tau dynamics in substance-specific ways. Alcohol and opioids promote Tau hyperphosphorylation and fragmentation via kinases like GSK-3β and CDK5 and proteases like caspase-3, leading to neuroinflammation. Stimulants and dissociatives disrupt insulin signaling and increase oxidative stress, exacerbating Tau pathology. Cannabinoids and psychedelics may protect by modulating kinase activity and reducing inflammation; psilocybin and harmine decrease Tau phosphorylation in animal models. Tau emerges as a convergent target in substance-related cognitive disorders, offering a biomarker and therapeutic target.

Total Recall: Lateral Habenula and Psychedelics in the Study of Depression and Comorbid Brain Disorders

International Journal of Molecular Sciences September 7, 2020 Matas Vitkauskas, Ajay S. Mathuru 4 citations

Depression affects millions worldwide. Recent research explores the lateral habenula's role in depression and the potential of psychedelics like psilocybin and ketamine as treatments. Clinical trials are testing deep brain stimulation of the habenula and psychedelic therapies targeting the serotonergic system. Early results are promising but require cautious optimism; more animal studies in naturalistic settings, larger human trials with better neuroimaging, and understanding of genetic and molecular factors underlying comorbid disorders are needed. Advances in cerebral organoids may accelerate progress. This review covers developments in these areas and discusses future directions.